Update on Research: Gene Therapy

The goal of this workshop is  to give families information they need to plan realistically for a  future where gene therapy could be an option. Let us talk openly about  the challenges and the possibilities of gene therapy for CdLS. Join  Medical Director, Dr. Antonie Kline; Research Committee Member, Dr. Art  Lander; and Dr. David Litwack from Prevail Therapeutics to review  potential hurdles and side effects, as well as any clinical trials that  may happen in the future.